Study Of An Investigational Drug For Becker Muscular Dystrophy
Seeking boys and men aged 12-50 with Becker Muscular Dystrophy for a study of the safety and effectiveness of an investigational drug to prevent muscle weakness.
Seeking boys and men aged 12-50 with Becker Muscular Dystrophy for a study of the safety and effectiveness of an investigational drug to prevent muscle weakness.
Seeking boys aged 4 to 16 for a study of an investigational drug to increase dystrophin protein levels in muscles.
Seeking men and women with upper limb spasticity that affects the movement in their arms and/or hands for a study comparing two treatments that have already been approved by the Food and Drug Administration (FDA).
Seeking adults aged 18 and older who either have Facioscapulohumeral Muscular Dystrophy (FSHD) or are healthy volunteers for a study to identify genetic biomarkers for the disease and better understand what causes it, and why symptoms vary widely among people who have it.
Seeking boys and men with Duchenne muscular dystrophy (DMD) or Becker Muscular Dystrophy (BMD) to provide samples including blood, plasma, serum, urine, as well as the remainders of tissue samples collected as part of their usual clinical care for a biorepository.
Seeking male participants aged 10-21 years of age who have been diagnosed with Duchenne Muscular Dystrophy (DMD) for participation in an imaging study.
Seeking men and women whose doctor has recommended surgery to relieve pain resulting from damage to a disc in their back being pushed out of place (herniated) for a study of an investigational device to prevent the disc from reherniating.
This study is intended to collect data from medical records on patients who have Duchenne Muscular Dystrophy
Seeking adults with degenerative spondylolisthesis with lumbar spinal stenosis whose doctors have recommended back surgery to address the pressure on your spinal cord or spinal nerves
Seeking men and women with moderate to severe rheumatoid arthritis that has not responded or has stopped responding to biologic or disease-modifying Anti-Rheumatic drugs for a study of an investigational device.
Seeking men and women whose active systemic lupus erythematosus (SLE) is being treated with non-biologic therapy for a study of an investigational drug.
Seeking men and women whose rheumatoid arthritis has not responded to TNF-biologic treatment for a study comparing two different types of treatments (non-TNFi-biologic and tsDMARDs).
Seeking men and women whose broken arms or legs will need to be treated with surgery for a study of what treatment practices best prevent infection.
Seeking adults who have inflammatory arthritis and who are willing to provide data by answering questionnaires, giving a blood sample and donating leftover tissue samples for a study to help researchers better understand inflammatory arthritis.
This is a registry to collect medical record information from people living with Multiple Sclerosis (MS) to better understand the disease and develop new treatments